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CLINICAL_TRIALS trial_result · 2017-11-24

Clinical Trial Update: Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy [Phase 1]

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Summary

Phase 1 intramuscular gene transfer trial using rAAVrh74.MCK.Micro-Dystrophin for Duchenne Muscular Dystrophy has completed.

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Diseases / indications

Drugs mentioned

  • rAAVrh74.MCK.Micro-Dystrophin

Snippet

Sponsor: Jerry R. Mendell | Conditions: Duchenne Muscular Dystrophy | Phase 1 | Status: COMPLETED