Duchenne Muscular Dystrophy
📧 Sign up to get email alerts when something new happens for Duchenne Muscular Dystrophy.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophy [Phase 2]
A Phase 2 historically controlled trial evaluating corticosteroids in young boys with Duchenne Muscular Dystrophy has completed with results…
-
CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy Consumption [NA]
A completed clinical trial evaluated kinesiology taping for its impact on performance, gait characteristics, and energy consumption in Duche…
-
CLINICAL_TRIALS trial_result · 2018-04-19Clinical Trial Update: L-citrulline and Metformin in Duchenne's Muscular Dystrophy [Phase 3]
A Phase 3 clinical trial evaluating the combination of L-citrulline and metformin for Duchenne muscular dystrophy has completed. The study w…
-
CLINICAL_TRIALS trial_result · 2018-04-05Clinical Trial Update: Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular Dystrophy
NHGRI-funded clinical trial update examining the relationship between hope, uncertainty, and coping efficacy among mothers of children with …
-
CLINICAL_TRIALS trial_result · 2018-03-21Clinical Trial Update: Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy [Phase 2]
Phase 2 trial of Revatio (sildenafil) for Duchenne and Becker muscular dystrophy was terminated; results were posted in 2018.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2018-02-01Clinical Trial Update: Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients [NA]
A completed clinical trial evaluated the effects of eicosapentaenoic acid (EPA) and docosahexaenoic acid (DHA) on inflammation and metabolic…
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort [Phase 1]
An open-label, long-term extension study assessed the safety and tolerability of deflazacort in Duchenne Muscular Dystrophy; the trial has c…
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.
A prospective natural history study of Duchenne Muscular Dystrophy sponsored by BioMarin has been terminated.
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy [Phase 1, Phase 2]
A Phase 1/2 study of PRO045 in Duchenne muscular dystrophy has been terminated. The termination status is indicated in the trial update.
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD) [Phase 2]
Open-label extension study of PRO044 in Duchenne muscular dystrophy (Phase 2) has been terminated.
-
CLINICAL_TRIALS trial_result · 2017-11-24Clinical Trial Update: Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy [Phase 1]
Phase 1 intramuscular gene transfer trial using rAAVrh74.MCK.Micro-Dystrophin for Duchenne Muscular Dystrophy has completed.
-
CLINICAL_TRIALS trial_result · 2017-10-16Clinical Trial Update: A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD) [Phase 2]
A Phase 2 study evaluating two doses of GSK2402968 in Duchenne muscular dystrophy has completed, with results posted in October 2017.
-
CLINICAL_TRIALS trial_result · 2017-08-18Clinical Trial Update: A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy [Phase 1]
Clinical trial update reporting completion of a Phase 1 pharmacokinetic study of oral deflazacort in children and adolescents with Duchenne …
-
CLINICAL_TRIALS trial_result · 2017-07-18Clinical Trial Update: A Double-blind, Escalating Dose, Randomized, Placebo-controlled Study Assessing PK, Safety, Tolerability in Non-ambulant DMD Subjects [Phase 1]
A Phase 1, double-blind, escalating-dose, randomized, placebo-controlled study in non-ambulant Duchenne muscular dystrophy patients evaluati…
-
CLINICAL_TRIALS trial_result · 2017-04-11Clinical Trial Update: Virtual Reality in Individuals With Duchenne Muscular Dystrophy [NA]
A clinical trial evaluating virtual reality for individuals with Duchenne Muscular Dystrophy has completed.
-
CLINICAL_TRIALS trial_result · 2017-03-23Clinical Trial Update: Open Label Study of GSK2402968 in Subjects With Duchenne Muscular Dystrophy [Phase 3]
Open-label Phase 3 trial of GSK2402968 for Duchenne muscular dystrophy has been terminated.
-
CLINICAL_TRIALS trial_result · 2017-03-21Clinical Trial Update: Cardiomyopathy in DMD: Lisinopril vs. Losartan [NA]
This entry notes a completed clinical trial comparing lisinopril versus losartan for cardiomyopathy in Duchenne muscular dystrophy, with res…
-
CLINICAL_TRIALS trial_result · 2017-03-01Clinical Trial Update: A Study of Tadalafil for Duchenne Muscular Dystrophy [Phase 3]
Phase 3 trial for tadalafil in Duchenne muscular dystrophy was terminated; results posted in 2017.
-
CLINICAL_TRIALS trial_result · 2017-01-18Clinical Trial Update: This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy
A completed clinical trial aimed at gathering more information about non-ambulatory boys and men with Duchenne muscular dystrophy.
-
CLINICAL_TRIALS trial_result · 2016-11-07Clinical Trial Update: A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the Potential for IV Dosing as an Alternative Route of Administration [Phase 2]
Phase I/II open-label escalating-dose pilot study of subcutaneous Drisapersen in Duchenne muscular dystrophy to assess safety, tolerability,…
-
CLINICAL_TRIALS trial_result · 2016-10-14Clinical Trial Update: Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy [Phase 2]
Phase 2 clinical trial of ACE-031 in Duchenne muscular dystrophy has been terminated with results posted in 2016.
-
CLINICAL_TRIALS trial_result · 2016-10-04Clinical Trial Update: Myocardial Involvement in Carriers of Duchenne Muscular Dystrophy: An MRI-study
This completed MRI study examined myocardial involvement in carriers of Duchenne muscular dystrophy. It aimed to understand potential heart …
-
CLINICAL_TRIALS trial_result · 2016-08-11Clinical Trial Update: A Device for Rapid, Painless, Bedside Muscle Evaluation of Children
This clinical trial update reports the completion of a study evaluating a rapid, painless bedside device for assessing muscle function in ch…
-
CLINICAL_TRIALS trial_result · 2016-03-24Clinical Trial Update: Electrical Impedance Myography and Ultrasound as Biomarkers of Duchenne Muscular Dystrophy
A completed study evaluating electrical impedance myography and ultrasound as potential biomarkers for Duchenne Muscular Dystrophy.
-
CLINICAL_TRIALS trial_result · 2016-02-03Clinical Trial Update: Mother-caregivers of Children With Duchenne Muscular Dystrophy [NA]
This entry reports on a completed clinical trial focusing on mother-caregivers of children with Duchenne Muscular Dystrophy. The sponsor is …