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CLINICAL_TRIALS trial_result · 2017-08-18

Clinical Trial Update: A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy [Phase 1]

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Summary

Clinical trial update reporting completion of a Phase 1 pharmacokinetic study of oral deflazacort in children and adolescents with Duchenne muscular dystrophy.

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Diseases / indications

Drugs mentioned

  • EMFLAZA (deflazacort)

Snippet

Sponsor: PTC Therapeutics | Conditions: Duchenne Muscular Dystrophy | Phase 1 | Status: COMPLETED