Cystic Fibrosis
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Sign up freeTop drugs studied for this disease
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FDA approval · 2025-09-25FDA Approved: ALYFTREK — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for Alyftrek (vanzacaftor, tezacaftor, and deutivacaftor) from Vertex Pharmaceuticals Incorporated.
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FDA approval · 2025-09-25FDA Approved: ORKAMBI — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for ORKAMBI (lumacaftor and ivacaftor) from Vertex Pharmaceuticals Incorporated.
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FDA approval · 2025-09-25FDA Approved: ORKAMBI — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA supplemental approval for Orkambi (lumacaftor and ivacaftor) by Vertex Pharmaceuticals Incorporated.
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FDA approval · 2025-09-25FDA Approved: KALYDECO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for KALYDECO (ivacaftor) submitted by Vertex Pharmaceuticals Incorporated.
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FDA approval · 2025-09-25FDA Approved: KALYDECO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
The FDA has approved a supplemental application for KALYDECO (ivacaftor) from Vertex Pharmaceuticals.
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FDA approval · 2025-09-25FDA Approved: SYMDEKO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved Vertex's supplemental application for SYMDEKO (tezacaftor and ivacaftor). The approval updates the product labeling.
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CLINICAL_TRIALS research · 2025-09-25Clinical Trial Update: MAGNIFY - Pulmonary Magnetic Resonance Imaging for Cystic Fibrosis
Trial update for MAGNIFY, a pulmonary MRI study for cystic fibrosis, currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-09-24Clinical Trial Update: Efficacy of Simeox Airway Clearance Therapy in Children With Cystic Fibrosis [NA]
Clinical trial update on the efficacy of Simeox airway clearance therapy in children with cystic fibrosis; the study has completed.
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: Genetic Modifiers of Cystic Fibrosis (CF) Liver Disease
Clinical trial update indicating an active, not-recruiting study at the University of North Carolina examining genetic modifiers of liver di…
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: Gene Modifiers of Cystic Fibrosis Lung Disease
This clinical trial update describes a study on gene modifiers of cystic fibrosis lung disease. The trial is currently not recruiting.
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CLINICAL_TRIALS trial_result · 2025-09-18Clinical Trial Update: Evaluation of the Evolution of Quality of Life in Relation to Naso-sinus Symptomatology Under Treatment With CFTE Modulators in Children Aged 6 to 11 Years With Cystic Fibrosis With Compatible Mutation
A completed clinical trial evaluating quality of life and nasal-sinus symptoms in children aged 6 to 11 with cystic fibrosis treated with CF…
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CLINICAL_TRIALS trial_result · 2025-09-18Clinical Trial Update: Validation of Therapeutic Efficacy Targeting the Splicing Variants in Cystic Fibrosis and CFTR Pathologies [NA]
Clinical trial evaluating therapies targeting splicing variants in cystic fibrosis and CFTR-related pathologies has been terminated.
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CLINICAL_TRIALS trial_result · 2025-09-16Clinical Trial Update: ELECTROVEST: Electro-Stimulation Vibratory Vest for Pulmonary Rehabilitation in Patients With Chronic Respiratory Diseases [NA]
A completed clinical trial evaluated the ELECTROVEST electro-stimulation vibratory vest for pulmonary rehabilitation in chronic respiratory …
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CLINICAL_TRIALS trial_result · 2025-09-12Clinical Trial Update: Cystic Fibrosis Blood Neutrophils [NA]
A completed clinical trial evaluating blood neutrophils in cystic fibrosis patients.
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CLINICAL_TRIALS trial_result · 2025-09-12Clinical Trial Update: Impact of Telerehabilitation Training on Pediatric Cystic Fibrosis Patients: An Exploratory Study [NA]
An exploratory study examining the impact of telerehabilitation training on pediatric cystic fibrosis patients has completed, presenting ear…
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CLINICAL_TRIALS trial_result · 2025-09-12Clinical Trial Update: Human Papillomavirus and Cervical Dysplasia in Women With Cystic Fibrosis [NA]
Clinical trial update indicates that the study on human papillomavirus infection and cervical dysplasia in women with cystic fibrosis has co…
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: Trikafta in Cystic Fibrosis Patients [Phase 2]
A Phase 2 clinical trial of Trikafta in cystic fibrosis patients has completed and posted results.
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CLINICAL_TRIALS research · 2025-09-08Clinical Trial Update: Muscle Fatigue in People With Cystic Fibrosis: Insight From a Mobile App
A clinical trial is recruiting to study muscle fatigue in people with cystic fibrosis using data collected from a mobile app.
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CLINICAL_TRIALS trial_result · 2025-09-08Clinical Trial Update: Upper Extremity Exercise Capacity, Muscle Oxygenation, and Balance in Pediatric CF and PCD
A pediatric trial evaluating upper-extremity exercise capacity, muscle oxygenation, and balance in cystic fibrosis and primary ciliary dyski…
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CLINICAL_TRIALS trial_result · 2025-09-05Clinical Trial Update: Pharmacokinetic and Pharmacodynamic Analysis of Ceftaroline in Children and Adolescents With Cystic Fibrosis [Phase 4]
This Phase 4 study reports pharmacokinetic and pharmacodynamic analyses of ceftaroline in children and adolescents with cystic fibrosis. The…
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CLINICAL_TRIALS trial_result · 2025-09-05Clinical Trial Update: A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy [Phase 3]
A Phase 3 clinical trial update for VX-121 combination therapy in cystic fibrosis notes long-term safety and efficacy monitoring, with the s…
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CLINICAL_TRIALS trial_result · 2025-09-04Clinical Trial Update: Determination of the Predictive Factors in the Reversibility or the Aggravation in the Disorders of the Glucose Metabolism in Cystic Fibrosis Patients [NA]
A completed clinical trial assessing predictive factors for reversibility or progression of glucose metabolism disorders in cystic fibrosis …
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CLINICAL_TRIALS trial_result · 2025-09-03Clinical Trial Update: Safety, Tolerability, and Pharmacokinetics of Multiple Dose Combinations of SION-451 and Complementary Modulators SION-2222 and SION-109 in Healthy Participants. [Phase 1]
Phase 1 clinical trial update evaluating safety, tolerability, and pharmacokinetics of multiple-dose combinations of SION-451 with SION-2222…
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CLINICAL_TRIALS research · 2025-09-03Clinical Trial Update: Continuous Glucose Monitoring and OGTT Screen for Cystic Fibrosis Related Diabetes in Cystic Fibrosis
This Clinical Trials update indicates that a study assessing continuous glucose monitoring and oral glucose tolerance test screening for cys…
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CLINICAL_TRIALS research · 2025-08-29Clinical Trial Update: Ensuring Access to Optimal Therapy in CF: The ENACT Study [Phase 4]
A Phase 4 clinical trial named ENACT in cystic fibrosis is currently recruiting, focusing on ensuring access to optimal therapy for CF patie…