Cystic Fibrosis
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CLINICAL_TRIALS trial_result · 2024-08-22Clinical Trial Update: Reproducibility of Virtual Exercise Assessments Versus Face-to-face Exercise Testing in Adults With Cystic Fibrosis [NA]
This clinical trial update examines how reproducible virtual exercise assessments are compared with in-person exercise testing in adults wit…
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CLINICAL_TRIALS research · 2024-08-12Clinical Trial Update: Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children
This clinical trial studies the biological and clinical effects of significantly corrected CFTR function in infants and young children with …
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CLINICAL_TRIALS trial_result · 2024-08-09Clinical Trial Update: Impact of Rifabutin on the Pharmacokinetics of Elexacaftor/Tezacaftor/Ivacaftor [Phase 4]
A Phase 4 trial evaluated how rifabutin alters the pharmacokinetics of the cystic fibrosis TRIKAFTA combo (elexacaftor/tezacaftor/ivacaftor)…
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CLINICAL_TRIALS trial_result · 2024-08-09Clinical Trial Update: Cystic Fibrosis and Gut Dysmotility: The Effect of Polyethylene Glycol (PEG) on Intestinal Transit [Phase 4]
Phase 4 trial assessing the effect of polyethylene glycol on intestinal transit in people with cystic fibrosis and gut dysmotility; results …
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CLINICAL_TRIALS trial_result · 2024-08-09Clinical Trial Update: Neuromodulation for Children With Cystic Fibrosis Experiencing Chronic Abdominal Pain [NA]
A terminated pediatric trial evaluated neuromodulation for chronic abdominal pain in children with cystic fibrosis; results were posted in 2…
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CLINICAL_TRIALS research · 2024-08-09Clinical Trial Update: Glucose Monitoring in Youth With Cystic Fibrosis During Pulmonary Exacerbations
This clinical trial update indicates that a study evaluating glucose monitoring in youth with cystic fibrosis during pulmonary exacerbations…
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CLINICAL_TRIALS trial_result · 2024-08-07Clinical Trial Update: MN4000 for Treatment of CF and MND Patients in the Home Setting [NA]
Results for a completed clinical trial (NCT03797677) evaluating MN4000 for home-based treatment of cystic fibrosis and motor neuron disease …
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CLINICAL_TRIALS trial_result · 2024-08-01Clinical Trial Update: Evaluation of Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) in Cystic Fibrosis Subjects Without an F508del Mutation [Phase 3]
A Phase 3 trial evaluating the efficacy and safety of the triple-combination CFTR modulator elexacaftor/tezacaftor/ivacaftor in cystic fibro…
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CLINICAL_TRIALS research · 2024-07-30Clinical Trial Update: Breath Analysis and Arterial Stiffness in Patients With Respiratory Diseases
This clinical trial update notes that the breath analysis and arterial stiffness study in patients with various respiratory diseases is curr…
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CLINICAL_TRIALS trial_result · 2024-07-23Clinical Trial Update: Study to Evaluate Symptoms of Exocrine Pancreatic Insufficiency in Adult Participants With Cystic Fibrosis or Chronic Pancreatitis Treated With Creon [Phase 4]
Phase 4 study evaluating symptoms of exocrine pancreatic insufficiency in adults with cystic fibrosis or chronic pancreatitis treated with C…
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CLINICAL_TRIALS trial_result · 2024-07-22Clinical Trial Update: A Comprehensive Approach To Relief Of Digestive Symptoms In Cystic Fibrosis: CARDS-CF
A clinical trial called CARDS-CF evaluated a comprehensive approach to relieving digestive symptoms in cystic fibrosis. The study status is …
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CLINICAL_TRIALS research · 2024-07-18Clinical Trial Update: Immune Profiles in CF Fungal Infection
A completed clinical trial update examining immune profiles in cystic fibrosis patients with fungal infections, including allergic bronchopu…
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CLINICAL_TRIALS trial_result · 2024-07-16Clinical Trial Update: Study to Evaluate Adverse Events and Change in Disease Activity With Oral Capsules of Galicaftor/Navocaftor/ABBV-119 or Galicaftor/Navocaftor/ABBV-576 Combination Therapies in Adult Participants With Cystic Fibrosis [Phase 2]
Phase 2 trial evaluating adverse events and changes in disease activity in adults with cystic fibrosis for two fixed-dose combinations of ga…
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CLINICAL_TRIALS trial_result · 2024-07-03Clinical Trial Update: CFTR Modulators and Gastrointestinal Complications
A completed clinical trial evaluating CFTR modulator therapies and their gastrointestinal complications in cystic fibrosis patients.
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CLINICAL_TRIALS research · 2024-07-03Clinical Trial Update: Xylitol vs Saline Nasal Irrigations in CF-CRS [NA]
This ClinicalTrials.gov entry reports a study comparing xylitol nasal irrigation to saline nasal irrigation for chronic rhinosinusitis in cy…
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CLINICAL_TRIALS trial_result · 2024-07-03Clinical Trial Update: The Effect of Breathing Exercise With Pinwheel on the Quality of Life in Children With Cystic Fibrosis Disease [NA]
A completed clinical trial investigated whether pinwheel-assisted breathing exercises can improve quality of life in children with cystic fi…
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CLINICAL_TRIALS trial_result · 2024-07-01Clinical Trial Update: Prednisone in Cystic Fibrosis Pulmonary Exacerbations [Phase 3]
Phase 3 trial update on prednisone for pulmonary exacerbations in cystic fibrosis; the study status is completed.
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CLINICAL_TRIALS research · 2024-07-01Clinical Trial Update: Effects of AD on VI in Patients With CF [NA]
A clinical trial titled 'Effects of AD on VI in Patients With CF' is currently recruiting for cystic fibrosis, sponsored by Cliniques univer…
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CLINICAL_TRIALS research · 2024-06-28Clinical Trial Update: Modulation by Sex Hormones of Inflammation and Susceptibility to Pseudomonas Aeruginosa in Cystic Fibrosis Airways
This entry reports a completed clinical trial investigating how sex hormones influence inflammation and susceptibility to Pseudomonas aerugi…
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CLINICAL_TRIALS trial_result · 2024-06-26Clinical Trial Update: Physical Activity, Exercise Capacity and Coronavirus Phobia of Adult Cystic Fibrosis Patients During COVID-19 Pandemic
This trial update reports on physical activity, exercise capacity, and coronavirus-related anxiety in adult cystic fibrosis patients during …
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CLINICAL_TRIALS trial_result · 2024-06-24Clinical Trial Update: Inhaled Sodium Nitrite as an Antimicrobial for Cystic Fibrosis [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating inhaled sodium nitrite as an antimicrobial for cystic fibrosis was terminated; results were posted in …
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CLINICAL_TRIALS trial_result · 2024-06-17Clinical Trial Update: Study to Assess the Safety and PK of Oral and IV Xenleta in Adults With Cystic Fibrosis [Phase 1]
A Phase 1 study assessed the safety and pharmacokinetics of oral and intravenous lefamulin (Xenleta) in adults with cystic fibrosis; results…
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CLINICAL_TRIALS trial_result · 2024-06-13Clinical Trial Update: A Study of VX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Who Are Homozygous for F508del, Heterozygous for F508del and a Gating (F/G) or Residual Function (F/RF) Mutation, or Have At Least 1 Other Triple Combination Responsive (TCR) CFTR Mutation and No F508del Mutation [Phase 3]
Phase 3 study evaluating VX-121 combination therapy in cystic fibrosis patients with multiple CFTR mutations has completed, with results pos…
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CLINICAL_TRIALS research · 2024-06-13Clinical Trial Update: Quality of Life and Gut Health in Pediatric Patients With Cystic Fibrosis [NA]
A pediatric clinical trial sponsored by Oslo University Hospital is evaluating quality of life and gut health in children with cystic fibros…
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CLINICAL_TRIALS trial_result · 2024-06-10Clinical Trial Update: A Phase 3 Study of VX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Heterozygous for F508del and a Minimal Function Mutation (F/MF) [Phase 3]
A Phase 3 study evaluating VX-121 combination therapy in cystic fibrosis patients who are heterozygous for F508del and a minimal function mu…