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CLINICAL_TRIALS research · 2024-08-12

Clinical Trial Update: Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children

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Summary

This clinical trial studies the biological and clinical effects of significantly corrected CFTR function in infants and young children with cystic fibrosis. The…

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Diseases / indications

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Sponsor: Sonya Heltshe | Conditions: Cystic Fibrosis | Status: RECRUITING