Cystic Fibrosis
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Sign up freeTop drugs studied for this disease
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FDA approval · 2024-12-20FDA Approved: ALYFTREK — Original Application (Vertex Pharmaceuticals Incorporated)
The FDA approves ALYFTREK, a triple combination therapy of vanzacaftor, tezacaftor, and deutivacaftor, in an original application for cystic…
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FDA approval · 2024-12-20FDA Approved: TRIKAFTA — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approves a supplemental application for TRIKAFTA (elexacaftor/tezacaftor/ivacaftor) from Vertex Pharmaceuticals Incorporated. The action…
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FDA approval · 2024-12-20FDA Approved: TRIKAFTA — Supplemental Application (Vertex Pharmaceuticals Incorporated)
The FDA approved a supplemental application for TRIKAFTA (elexacaftor, tezacaftor, and ivacaftor) submitted by Vertex Pharmaceuticals, relat…
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CLINICAL_TRIALS trial_result · 2024-12-17Clinical Trial Update: Imipenem/Cilastatin/Relebactam Pharmacokinetics, Safety, and Outcomes in Adults and Adolescents With Cystic Fibrosis [Phase 4]
Phase 4 trial evaluating pharmacokinetics, safety, and outcomes of imipenem/cilastatin/relebactam in adults and adolescents with cystic fibr…
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CLINICAL_TRIALS trial_result · 2024-12-16Clinical Trial Update: Cefiderocol Pharmacokinetics in Adult Patients With Cystic Fibrosis [Phase 4]
This clinical trial update reports pharmacokinetic data for cefiderocol in adult patients with cystic fibrosis in a Phase 4 study.
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FDA approval · 2024-12-13FDA Approved: ORKAMBI — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for ORKAMBI (lumacaftor and ivacaftor) submitted by Vertex Pharmaceuticals. The action updates/expan…
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FDA approval · 2024-12-13FDA Approved: ORKAMBI — Supplemental Application (Vertex Pharmaceuticals Incorporated)
The FDA approved a supplemental application for ORKAMBI (lumacaftor and ivacaftor) from Vertex Pharmaceuticals Incorporated. This action con…
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CLINICAL_TRIALS trial_result · 2024-12-13Clinical Trial Update: Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of SPL84 in Patients with Cystic Fibrosis [Phase 2]
Phase 2 clinical trial evaluating SPL84 in cystic fibrosis is currently recruiting to assess safety, tolerability, pharmacokinetics, and pre…
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CLINICAL_TRIALS research · 2024-12-10Clinical Trial Update: Determinants of Daily Physical Activity Level in Patients With Cystic Fibrosis - Pilot Study Protocol [NA]
This document outlines a pilot study protocol investigating determinants of daily physical activity levels in people with cystic fibrosis.
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CLINICAL_TRIALS trial_result · 2024-12-06Clinical Trial Update: Efficacy of TOBI Podhaler vs. Tobramycin Inhalation Solution
Study comparing TOBI Podhaler (tobramycin inhalation powder) with Tobramycin Inhalation Solution in cystic fibrosis was terminated; results …
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CLINICAL_TRIALS research · 2024-12-06Clinical Trial Update: Lung Transplant READY CF 2: CARING CF Ancillary RCT [NA]
The document reports a recruiting status for a cystic fibrosis trial titled Lung Transplant READY CF 2: CARING CF Ancillary RCT, sponsored b…
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CLINICAL_TRIALS trial_result · 2024-12-04Clinical Trial Update: "Safety, Tolerability and Pharmacokinetics of MP-376 Administered for 14 Days to Stable Pediatric (CF) Patients" [Phase 1]
Phase 1 study evaluating safety, tolerability, and pharmacokinetics of MP-376 administered for 14 days to stable pediatric patients with cys…
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CLINICAL_TRIALS trial_result · 2024-12-04Clinical Trial Update: Safety, Pharmacokinetic and Pharmacodynamic Study of MP-376 in Patients With Cystic Fibrosis [Phase 1]
Phase 1 safety, pharmacokinetic and pharmacodynamic study of MP-376 in patients with cystic fibrosis has completed.
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CLINICAL_TRIALS trial_result · 2024-11-26Clinical Trial Update: Impact of Discontinuing Dornase Alfa in People With CF on Highly Effective CFTR Modulator Therapy-A SIMPLIFY Sub-Study [NA]
The SIMPLIFY sub-study reports results on discontinuing Dornase alfa in people with cystic fibrosis who are on highly effective CFTR modulat…
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CLINICAL_TRIALS trial_result · 2024-11-26Clinical Trial Update: NETwork of Linoleic Acid Supplementation in Cystic Fibrosis [NA]
Karolinska Institutet completed a clinical trial evaluating linoleic acid supplementation in cystic fibrosis.
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CLINICAL_TRIALS research · 2024-11-25Clinical Trial Update: A Phase 1/2 Trial of SP-101 for the Treatment of Cystic Fibrosis (CF) [Phase 1, Phase 2]
SP-101 is being evaluated in a Phase 1/2 clinical trial for cystic fibrosis. The study is currently recruiting.
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CLINICAL_TRIALS research · 2024-11-21Clinical Trial Update: Monitoring Response to Orkambi in Cystic Fibrosis Lung Disease by Inhaled Xenon MRI
A clinical trial update describes monitoring the response of cystic fibrosis lung disease to Orkambi using inhaled xenon MRI.
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CLINICAL_TRIALS trial_result · 2024-11-21Clinical Trial Update: BEGIN Novel ImagiNG Biomarkers [Phase 4]
Phase 4 clinical trial update for BEGIN Novel ImagiNG Biomarkers sponsored by Children's Hospital Medical Center, Cincinnati, investigating …
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CLINICAL_TRIALS trial_result · 2024-11-19Clinical Trial Update: Airway Clearance for Pediatric and Adult Cystic Fibrosis Patients Using a Portable Intra-Pulmonary Percussion Device [NA]
A terminated clinical trial evaluating a portable intra-pulmonary percussion device for airway clearance in pediatric and adult cystic fibro…
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CLINICAL_TRIALS research · 2024-11-18Clinical Trial Update: Resting Energy Expenditure in Patients With Cystic Fibrosis: A Pilot Study [NA]
Clinical trial update noting termination of a pilot study on resting energy expenditure in patients with cystic fibrosis.
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CLINICAL_TRIALS research · 2024-11-14Clinical Trial Update: FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
FLOWER is a longitudinal epidemiology study by xCures to follow outcomes across multiple rare diseases, and the study is currently recruitin…
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CLINICAL_TRIALS trial_result · 2024-11-13Clinical Trial Update: Safety, Tolerability, and Pharmacokinetics of ARCT-032 in Healthy Adult Subjects and Adults With Cystic Fibrosis. [Phase 1]
This clinical trial update reports safety, tolerability, and pharmacokinetics data for ARCT-032 in healthy adults and adults with cystic fib…
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CLINICAL_TRIALS research · 2024-11-06Clinical Trial Update: Identification of Dysglycemia With Continuous Glucose Monitoring to Assess Clinical Evolution in Cystic Fibrosis
A clinical trial is exploring the use of continuous glucose monitoring to identify dysglycemia and track clinical evolution in individuals w…
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CLINICAL_TRIALS trial_result · 2024-10-30Clinical Trial Update: The Effect of Telenursing on Self-efficacy and Treatment Adherence in Children With Cystic Fibrosis [NA]
Completed clinical trial evaluating the effect of telenursing on self-efficacy and treatment adherence in children with cystic fibrosis.
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CLINICAL_TRIALS research · 2024-10-28Clinical Trial Update: COVID-19 Antibody Responses In Cystic Fibrosis
A clinical trial update indicating a study on COVID-19 antibody responses in cystic fibrosis patients is currently active but not recruiting…