Cerebral Adrenoleukodystrophy

Top drugs studied for this disease

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CLINICAL_TRIALS trial_result · 2025-07-02
Clinical Trial Update: A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
Clinical trial update for cerebral adrenoleukodystrophy (CALD) patients treated with elivaldogene autotemcel; the study is currently recruit…
CLINICAL_TRIALS trial_result · 2025-05-30
Clinical Trial Update: MT2022-01: MSCs for ALD [Phase 1]
The Phase 1 trial MT2022-01 evaluating mesenchymal stem cells for Cerebral Adrenoleukodystrophy is currently suspended. The update provides …
CLINICAL_TRIALS trial_result · 2025-02-20
Clinical Trial Update: Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
This clinical trial update provides long-term follow-up data for participants with cerebral adrenoleukodystrophy who were treated with the L…
CLINICAL_TRIALS trial_result · 2024-05-24
Clinical Trial Update: A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD) [Phase 3]
A Phase 3 gene therapy trial for cerebral Adrenoleukodystrophy has completed, with results posted in May 2024. The update highlights the tri…
CLINICAL_TRIALS trial_result · 2023-07-18
Clinical Trial Update: A Clinical Study in Male Pediatric Patients With Cerebral X-linked Adrenoleukodystrophy (Cald) to Assess the Effects of MIN-102 Treatment on Disease Progression Prior to Human Stem Cell Transplant (HSCT) [Phase 2]
A Phase 2 clinical trial evaluating MIN-102 in male pediatric patients with cerebral X-linked adrenoleukodystrophy prior to human stem cell …
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