Clinical Trial Update: A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD) [Phase 3]

View source ↗

Summary

A Phase 3 gene therapy trial for cerebral Adrenoleukodystrophy has completed, with results posted in May 2024. The update highlights the trial's efficacy and sa…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Cerebral Adrenoleukodystrophy

Drugs mentioned

• CALD Gene Therapy

Snippet

Sponsor: Genetix Biotherapeutics Inc. | Conditions: Cerebral Adrenoleukodystrophy (CALD) | Phase 3 | Status: COMPLETED | Results posted: 2024-05-24