Cerebral Adrenoleukodystrophy

• CLINICAL_TRIALS research · 2025-11-17
  Clinical Trial Update: A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy [Phase 3]

  Phase 3 clinical trial evaluating Leriglitazone for efficacy and safety in adult male subjects with cerebral adrenoleukodystrophy is current…

• CLINICAL_TRIALS trial_result · 2025-07-02
  Clinical Trial Update: A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  Clinical trial update for cerebral adrenoleukodystrophy (CALD) patients treated with elivaldogene autotemcel; the study is currently recruit…

• CLINICAL_TRIALS trial_result · 2025-05-30
  Clinical Trial Update: MT2022-01: MSCs for ALD [Phase 1]

  The Phase 1 trial MT2022-01 evaluating mesenchymal stem cells for Cerebral Adrenoleukodystrophy is currently suspended. The update provides …

• CLINICAL_TRIALS research · 2025-05-08
  Clinical Trial Update: Adrenoleukodystrophy National Registry Study

  A clinical trial registry update indicates a National Registry Study for Adrenoleukodystrophy is currently recruiting.

• CLINICAL_TRIALS trial_result · 2025-02-20
  Clinical Trial Update: Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

  This clinical trial update provides long-term follow-up data for participants with cerebral adrenoleukodystrophy who were treated with the L…

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• CLINICAL_TRIALS trial_result · 2024-05-24
  Clinical Trial Update: A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD) [Phase 3]

  A Phase 3 gene therapy trial for cerebral Adrenoleukodystrophy has completed, with results posted in May 2024. The update highlights the tri…

• CLINICAL_TRIALS trial_result · 2023-07-18
  Clinical Trial Update: A Clinical Study in Male Pediatric Patients With Cerebral X-linked Adrenoleukodystrophy (Cald) to Assess the Effects of MIN-102 Treatment on Disease Progression Prior to Human Stem Cell Transplant (HSCT) [Phase 2]

  A Phase 2 clinical trial evaluating MIN-102 in male pediatric patients with cerebral X-linked adrenoleukodystrophy prior to human stem cell …

• CLINICAL_TRIALS research · 2022-04-25
  Clinical Trial Update: A Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD) [Phase 2, Phase 3]

  Phase 2/3 study evaluating hematopoietic stem cells transduced with Lenti-D lentiviral vector for cerebral adrenoleukodystrophy (CALD) has c…

• CLINICAL_TRIALS withdrawal · 2017-12-02
  Clinical Trial Update: MT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD) [Phase 1]

  A Phase 1 trial of MT2014-14 IT-MSC for advanced cerebral adrenoleukodystrophy has been withdrawn.