Bone Marrow Failure Syndromes
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC [EARLY_Phase 1]
An early-phase expanded-access protocol evaluating CD3+/CD19+ depleted peripheral blood stem cells for leukemia and related immunodeficiency…
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CLINICAL_TRIALS research · 2026-01-07Clinical Trial Update: Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders [Phase 1, Phase 2]
A Phase 1/2 clinical trial at Washington University evaluates reduced-intensity conditioning and familial HLA-mismatched bone marrow transpl…
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CLINICAL_TRIALS trial_result · 2025-12-08Clinical Trial Update: Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases [Phase 2]
A Phase 2 trial comparing treosulfan-based conditioning to busulfan-based conditioning in pediatric patients with non-malignant diseases has…
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CLINICAL_TRIALS trial_result · 2025-10-23Clinical Trial Update: Methadone as an Alternative Treatment for Children Underdoing HSCT [Phase 3]
Phase 3 trial evaluating methadone as an alternative treatment for children undergoing hematopoietic stem cell transplantation; the study is…
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CLINICAL_TRIALS research · 2025-05-20Clinical Trial Update: Fludarabine Based RIC for Bone Marrow Failure Syndromes [EARLY_Phase 1]
An early-phase 1 clinical trial evaluating fludarabine-based reduced-intensity conditioning for bone marrow failure syndromes is currently r…
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CLINICAL_TRIALS trial_result · 2023-08-31Clinical Trial Update: Nandrolone Decanoate in the Treatment of Telomeropathies [Phase 1, Phase 2]
Phase 1/2 clinical trial of nandrolone decanoate for telomeropathies, including aplastic anemia and bone marrow failure syndromes, has compl…
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CLINICAL_TRIALS trial_result · 2023-03-10Clinical Trial Update: Transplantation of Partially Mismatched Related or Matched Unrelated Bone Marrow for Patients With Refractory Severe Aplastic Anemia [Phase 2]
Phase 2 trial update on transplantation of partially mismatched related or matched unrelated bone marrow for refractory severe aplastic anem…
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CLINICAL_TRIALS trial_result · 2018-04-11Clinical Trial Update: Reduced Intensity Conditioning Using CD3+/CD19+ Depletion for Non Malignant Transplantable Diseases [Phase 2]
Phase 2 trial evaluating reduced intensity conditioning using CD3+/CD19+ depletion for non-malignant transplantable diseases completed with …
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CLINICAL_TRIALS trial_result · 2015-04-15Clinical Trial Update: Unrelated Donor Transplant for Malignant and Non-Malignant Disorders [Phase 2]
Phase 2 trial of unrelated donor transplantation for malignant and non-malignant hematologic disorders; the study status is terminated.
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CLINICAL_TRIALS trial_result · 2011-02-17Clinical Trial Update: Comparison of Cy-Atg Vs Cy-Flu-Atg for the Conditioning Therapy in Allo-HCT [Phase 3]
Phase 3 trial comparing conditioning regimens Cy-Atg and Cy-Flu-Atg for allogeneic hematopoietic cell transplantation has completed. This st…
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CLINICAL_TRIALS research · 2010-04-21Clinical Trial Update: Identifying Characteristics of Bone Marrow Failure Syndromes
This clinical trial update describes a study to identify characteristics of bone marrow failure syndromes and related hematologic conditions…