Clinical Trial Update: Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases [Phase 2]

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Summary

A Phase 2 trial comparing treosulfan-based conditioning to busulfan-based conditioning in pediatric patients with non-malignant diseases has completed.

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Diseases / indications

• Bone Marrow Failure Syndromes
• Hemoglobinopathies
• Immunodeficiency Diseases
• Inborn Errors of Metabolism

Drugs mentioned

• BUSULFAN (Busulfan)
• Treosulfan (treosulfan)

Snippet

Sponsor: medac GmbH | Conditions: Primary Immunodeficiencies, Inborn Errors of Metabolism | Phase 2 | Status: COMPLETED