Bone Marrow Failure Syndromes
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC [EARLY_Phase 1]
An early-phase expanded-access protocol evaluating CD3+/CD19+ depleted peripheral blood stem cells for leukemia and related immunodeficiency…
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CLINICAL_TRIALS research · 2026-01-07Clinical Trial Update: Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders [Phase 1, Phase 2]
A Phase 1/2 clinical trial at Washington University evaluates reduced-intensity conditioning and familial HLA-mismatched bone marrow transpl…
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CLINICAL_TRIALS research · 2025-05-20Clinical Trial Update: Fludarabine Based RIC for Bone Marrow Failure Syndromes [EARLY_Phase 1]
An early-phase 1 clinical trial evaluating fludarabine-based reduced-intensity conditioning for bone marrow failure syndromes is currently r…
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CLINICAL_TRIALS research · 2010-04-21Clinical Trial Update: Identifying Characteristics of Bone Marrow Failure Syndromes
This clinical trial update describes a study to identify characteristics of bone marrow failure syndromes and related hematologic conditions…