Beta Thalassemia Major
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: ß-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene [Phase 1]
Phase 1 clinical trial update for beta-thalassemia major using autologous CD34+ cells transduced with TNS9.3.55, a lentiviral vector encodin…
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CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: Risk Factors Affecting Growth in Thalassemic Children at AUCH
A clinical trial at Assiut University is investigating risk factors affecting growth in children with beta-thalassemia major. The study is c…
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major [Phase 2]
Phase 2 safety and efficacy study of CS-101 for beta-thalassemia major, with the study not yet recruiting.
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Gonadal Function in Thalassemic Patient
A clinical trial investigates gonadal function in patients with beta-thalassemia major; the study is currently not yet recruiting.
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CLINICAL_TRIALS research · 2025-10-06Clinical Trial Update: Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD [NA]
A clinical trial is currently recruiting to evaluate physiological and psychological factors involved in exercise intolerance in patients wi…
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CLINICAL_TRIALS research · 2025-10-02Clinical Trial Update: Body Composition in Pediatric Patients With Thalassemia Major
This document notes a clinical trial update for a pediatric study on body composition in patients with beta-thalassemia major. It is sponsor…
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CLINICAL_TRIALS research · 2025-09-02Clinical Trial Update: A Clinical Study of Ultra-transplantation for the Treatment of Major Thalassemia Scheme [NA]
This clinical trial update indicates a study evaluating ultra-transplantation for the treatment of major beta-thalassemia, and the study is …
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CLINICAL_TRIALS research · 2025-08-12Clinical Trial Update: T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias [Phase 1, Phase 2]
This clinical trials update notes that a T-cell depleted alternative donor bone marrow transplant for sickle cell disease and other anemias …
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CLINICAL_TRIALS research · 2025-08-08Clinical Trial Update: Effect of Incentive Respiratory Training on Pulmonary Functions and Functional Capacity in Children With B-thalassemia Major [NA]
This clinical trial update reports ongoing recruitment for a study evaluating incentive respiratory training with an incentive spirometer to…
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CLINICAL_TRIALS research · 2025-06-04Clinical Trial Update: A Real-World Study of β-Thalassemia Major Treatment With Luspatercept in Taiwan
This is a real-world, Taiwan-based study evaluating luspatercept for beta-thalassemia major, currently active but not recruiting.
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CLINICAL_TRIALS research · 2025-05-30Clinical Trial Update: Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta Thalassemia [Phase 2]
Phase 2 clinical trial evaluating different doses of thalidomide in transfusion-dependent beta-thalassemia is currently recruiting.
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CLINICAL_TRIALS research · 2025-05-20Clinical Trial Update: The Effect of Laughter Yoga in Beta Thalassaemia Major Patients: a Randomised Controlled Trial [NA]
An update on a randomized controlled trial evaluating laughter yoga in beta-thalassemia major patients. The study status is not yet recruiti…
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CLINICAL_TRIALS research · 2025-02-10Clinical Trial Update: Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major [EARLY_Phase 1]
This is an early-phase (Phase 1) clinical trial evaluating base-edited autologous hematopoietic stem cell transplantation for beta-thalassem…
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CLINICAL_TRIALS research · 2024-12-16Clinical Trial Update: Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemia [NA]
A clinical study investigating a 'super transplantation' approach for severe beta-thalassemia using haplo-identical donors is currently recr…
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CLINICAL_TRIALS research · 2024-11-29Clinical Trial Update: Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients [EARLY_Phase 1]
Early-phase clinical trial update evaluating safety and efficacy of β-globin–restored autologous hematopoietic stem cells in β-thalassemia m…
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CLINICAL_TRIALS research · 2024-06-20Clinical Trial Update: Inspiratory Muscle Training in Children With Beta Thalasemia [NA]
A clinical trial evaluating inspiratory muscle training in children with beta-thalassemia major is currently recruiting.
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CLINICAL_TRIALS research · 2024-06-14Clinical Trial Update: Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia [NA]
This entry describes a clinical trial evaluating a gene-modified autologous hematopoietic stem cell therapy for transfusion-dependent beta-t…
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CLINICAL_TRIALS research · 2019-02-20Clinical Trial Update: Sexual Maturation in β-Thalassemia Major Patients in Assiut University Hospital
This clinical trial update examines sexual maturation in beta-thalassemia major patients receiving chelation therapy at Assiut University Ho…
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CLINICAL_TRIALS research · 2017-04-26Clinical Trial Update: Benefits of Nigella Sativa in Children With Beta Thalassemia Major [EARLY_Phase 1]
An early-phase 1 clinical trial investigating Nigella Sativa for children with beta-thalassemia major, with the trial status not specified.
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CLINICAL_TRIALS research · 2017-04-25Clinical Trial Update: Study of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major [NA]
A clinical trial update evaluating Al-hijamah as a treatment for beta-thalassemia major in children; the current status is unknown.
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CLINICAL_TRIALS research · 2017-01-09Clinical Trial Update: Sperm DNA Damage in β-thalassemia Major: Is There a Role for Antioxidants? [Phase 1, Phase 2]
This clinical trial update investigates whether antioxidants can mitigate sperm DNA damage in men with beta-thalassemia major, spanning Phas…
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CLINICAL_TRIALS research · 2015-04-16Clinical Trial Update: Unrelated Umbilical Cord Blood Following HLA-haploidentical Hematopoietic Stem Cell Transplantation in Patients With β-thalassemia Major [NA]
ClinicalTrials.gov entry describes a study using unrelated umbilical cord blood after haploidentical hematopoietic stem cell transplantation…
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CLINICAL_TRIALS research · 2015-01-14Clinical Trial Update: An Algorithm to Start Iron Chelation in Minimally Transfused Young Beta-thalassemia Major Patients [Phase 2, Phase 3]
A clinical trial update describing a Phase 2/Phase 3 study evaluating an algorithm to start iron chelation in minimally transfused young pat…
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CLINICAL_TRIALS research · 2013-05-06Clinical Trial Update: B Memory Cell Response to Vaccination With the 13-valent Pneumococcal Conjugate Vaccine in Asplenic Individuals [Phase 4]
This clinical trial update describes a Phase 4 study evaluating B memory cell responses to the 13-valent pneumococcal conjugate vaccine in i…
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CLINICAL_TRIALS research · 2012-02-06Clinical Trial Update: Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload [Phase 2, Phase 3]
A Phase 2/3 clinical trial comparing the combination of deferasirox and deferiprone to the combination of deferiprone and deferoxamine (Desf…