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CLINICAL_TRIALS research · 2024-06-14

Clinical Trial Update: Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia [NA]

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Summary

This entry describes a clinical trial evaluating a gene-modified autologous hematopoietic stem cell therapy for transfusion-dependent beta-thalassemia and indic…

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Diseases / indications

Drugs mentioned

  • Gene-modified autologous hematopoietic stem cell therapy (gene-modified autologous hematopoietic stem cells)

Snippet

Sponsor: Shanghai BDgene Co., Ltd. | Conditions: β-thalassemia Major | NA | Status: RECRUITING