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CLINICAL_TRIALS research · 2025-02-10

Clinical Trial Update: Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major [EARLY_Phase 1]

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Summary

This is an early-phase (Phase 1) clinical trial evaluating base-edited autologous hematopoietic stem cell transplantation for beta-thalassemia major.

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Diseases / indications

Drugs mentioned

  • Base-edited autologous hematopoietic stem cell transplantation

Snippet

Sponsor: Children's Hospital of Fudan University | Conditions: Beta-Thalassemia | EARLY_Phase 1 | Status: ACTIVE_NOT_RECRUITING