Barth Syndrome
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Ph3b/4 Trial in Patients With Barth Syndrome [Phase 4]
Notes a Phase 3b/4 clinical trial in Barth Syndrome, sponsored by Stealth BioTherapeutics, that is not yet recruiting.
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CLINICAL_TRIALS research · 2025-02-14Clinical Trial Update: An Intermediate Size Expanded Access Protocol of Elamipretide
The update describes an intermediate-size expanded access protocol for elamipretide in patients with mitochondrial diseases, including Barth…