Barth Syndrome
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CLINICAL_TRIALS trial_result · 2024-04-16Clinical Trial Update: A Trial to Evaluate Safety, Tolerability and Efficacy of Elamipretide in Subjects With Barth Syndrome [Phase 2, Phase 3]
Phase 2/3 trial evaluating safety, tolerability, and efficacy of elamipretide in Barth syndrome completed with results posted in 2024.
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CLINICAL_TRIALS trial_result · 2017-01-10Clinical Trial Update: Exercise Training in Barth Syndrome [NA]
This update announces the completion of a clinical trial evaluating exercise training in Barth syndrome.