Clinical Trial Update: An Intermediate Size Expanded Access Protocol of Elamipretide

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Summary

The update describes an intermediate-size expanded access protocol for elamipretide in patients with mitochondrial diseases, including Barth syndrome.

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Diseases / indications

• Barth Syndrome
• Mitochondrial Disease

Drugs mentioned

• Elamipretide (elamipretide)

Snippet

Sponsor: Stealth BioTherapeutics Inc. | Conditions: Mitochondrial Diseases, Barth Syndrome | Status: AVAILABLE