Amyloidosis
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EMA approval · 2026-08-27EMA Authorised: Vyndaqel (tafamidis) — Pfizer Europe MA EEIG
European Medicines Agency authorises Vyndaqel (tafamidis) for Amyloidosis via Pfizer Europe MA EEIG.
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EMA approval · 2026-06-04EMA Authorised: Tegsedi (inotersen sodium) — Akcea Therapeutics Ireland Limited
Authorised: Tegsedi (inotersen sodium) by Akcea Therapeutics Ireland Limited for amyloidosis with orphan designation and accelerated assessm…
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EMA approval · 2026-06-03EMA Authorised: Vyndaqel (tafamidis) — Pfizer Europe MA EEIG
Authorised status for Vyndaqel (tafamidis) from EMA, with orphan designation, for amyloidosis.
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EMA approval · 2026-04-22EMA Authorised: Vyndaqel (tafamidis) — Pfizer Europe MA EEIG
The European Medicines Agency authorised Vyndaqel (tafamidis) for amyloidosis, with Pfizer Europe MA EEIG as the marketing authorisation hol…
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CLINICAL_TRIALS research · 2026-04-16Clinical Trial Update: NatiOnal Referral cenTEr Study of Transthyretin Amyloid Cardiomyopathy(ATTR) Patients on Tafamidis
A clinical trial at a national referral center is evaluating tafamidis in patients with transthyretin amyloid cardiomyopathy (ATTR-CM) and i…
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Characterizing Iodine-124 Evuzumitide (AT-01) in Systemic Amyloidosis [Phase 2]
A Phase 2 clinical trial update characterizing iodine-124 labeled Evuzumitide (AT-01) for systemic amyloidosis, including transthyretin amyl…
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CLINICAL_TRIALS trial_result · 2026-04-07Clinical Trial Update: Hereditary Transthyretin Amyloidosis Polyneuropathy in Patients With Carpal Tunnel Syndrome in Russia
This document reports the completion of a clinical trial investigating hereditary transthyretin amyloidosis with polyneuropathy in patients …
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CLINICAL_TRIALS research · 2026-03-30Clinical Trial Update: Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant [Phase 3]
This entry notes that Acoramidis is being evaluated in a Phase 3 ACT-EARLY prevention trial in asymptomatic carriers of pathogenic TTR varia…
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CLINICAL_TRIALS trial_result · 2026-03-16Clinical Trial Update: Diagnostic Utility of F-18 Florbetapir PET/MR in Peripheral Nerve Amyloidosis [Phase 1, Phase 2]
A completed Phase 1/Phase 2 study evaluating the diagnostic utility of the PET tracer F-18 Florbetapir in conjunction with MRI for periphera…
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CLINICAL_TRIALS trial_result · 2026-03-12Clinical Trial Update: Monitoring of Early Disease Progression in Hereditary Transthyretin Amyloidosis
Completed clinical trial update describing approaches to monitoring early disease progression in hereditary transthyretin amyloidosis. The s…
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CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: BE.Amycon Biobank & Data Registry UZ Leuven
A clinical trial registry update for the BE.Amycon Biobank & Data Registry at Universitaire Ziekenhuizen KU Leuven, focusing on amyloidosis …
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CLINICAL_TRIALS trial_result · 2026-02-17Clinical Trial Update: Phase 1/2a Study of Belantamab Mafodotin in Relapsed or Refractory AL Amyloidosis [Phase 1, Phase 2]
A Phase 1/2a clinical trial is investigating belantamab mafodotin for relapsed or refractory AL amyloidosis; the study is currently recruiti…
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CLINICAL_TRIALS trial_result · 2026-02-11Clinical Trial Update: Study of Olfactory Disorders in Patients With Cardiac Amyloidosis [NA]
A completed clinical trial conducted by Assistance Publique - Hôpitaux de Paris studied olfactory disorders in patients with cardiac amyloid…
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Expanded Access to Venetoclax
Expanded access to venetoclax is being offered for multiple hematologic cancers, including chronic lymphocytic leukemia, multiple myeloma, A…
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CLINICAL_TRIALS research · 2026-01-22Clinical Trial Update: HIBA-Institutional Registry of Amyloidosis
Clinical trial registry entry for the HIBA-Institutional Registry of Amyloidosis, sponsored by Hospital Italiano de Buenos Aires, currently …
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CLINICAL_TRIALS research · 2026-01-14Clinical Trial Update: Institutional Registry of Rare Diseases
An institutional registry for rare diseases sponsored by Hospital Italiano de Buenos Aires is currently recruiting. The registry includes am…
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CLINICAL_TRIALS research · 2025-12-26Clinical Trial Update: A Study Of Myocardial Stiffness In Amyloidosis With Magnetic Resonance Elastography
A Mayo Clinic-sponsored clinical trial is evaluating myocardial stiffness in amyloidosis using magnetic resonance elastography and is curren…
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CLINICAL_TRIALS research · 2025-12-24Clinical Trial Update: Generative AI Impact on Rheumatoid Arthritis Complications Diagnosis
A clinical trial in China is evaluating whether generative AI can improve the diagnosis of complications associated with rheumatoid arthriti…
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CLINICAL_TRIALS research · 2025-12-23Clinical Trial Update: Amyloidosis TTR Flow Reserve Evaluation [NA]
This clinical trial registry entry notes an ongoing study evaluating flow reserve in transthyretin amyloid cardiomyopathy, which is currentl…
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CLINICAL_TRIALS research · 2025-12-08Clinical Trial Update: Cancer and Aging Resilience Evaluation in Older Adults With Hematologic Malignancies: The CARE-Heme Registry
A registry study to evaluate cancer and aging resilience in older adults with hematologic malignancies, including multiple myeloma, amyloido…
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CLINICAL_TRIALS trial_result · 2025-12-05Clinical Trial Update: Daratumumab After Stem Cell Transplant in Treating Patients With Multiple Myeloma [Phase 2]
A Phase 2 clinical trial is evaluating daratumumab after stem cell transplant in patients with multiple myeloma. The study is currently acti…
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CLINICAL_TRIALS research · 2025-12-02Clinical Trial Update: Prevalence of Amyloidosis in Trauma Patients
An ongoing clinical trial is studying how common amyloidosis is among trauma patients and is currently recruiting.
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CLINICAL_TRIALS research · 2025-11-20Clinical Trial Update: Registry for Adults With Plasma Cell Disorders (PCD's)
Clinical trial registry update for adults with plasma cell disorders indicating active recruitment. The study is sponsored by UNC Lineberger…
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CLINICAL_TRIALS research · 2025-11-18Clinical Trial Update: [18F]FT8 PET Imaging in Immunoglobulin Light Chain Amyloidosis
This clinical trial is evaluating an 18F-labeled PET imaging tracer called [18F]FT8 for amyloidosis, including cardiac amyloidosis. The stud…
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CLINICAL_TRIALS research · 2025-11-14Clinical Trial Update: Molecular Imaging of Primary Amyloid Cardiomyopathy [NA]
A Brigham and Women's Hospital-sponsored clinical trial is investigating molecular imaging for primary amyloid cardiomyopathy. The study is …