Alpha-mannosidosis

• CLINICAL_TRIALS trial_result · 2026-01-07
  Clinical Trial Update: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis [Phase 2]

  Phase 2 trial update describing allogeneic hematopoietic cell transplantation for metabolic disorders and severe osteopetrosis, with the stu…

• CLINICAL_TRIALS trial_result · 2025-05-16
  Clinical Trial Update: Analysis of Velmanase Alfa (Lamzede®)'s Effects in the Body of Children With Alpha-Mannosidosis Under the Age 3

  This clinical trial update describes a study of Velmanase alfa (Lamzede) in children under 3 with Alpha-mannosidosis that is currently recru…

• CLINICAL_TRIALS trial_result · 2023-07-28
  Clinical Trial Update: Lamazym Aftercare Study [Phase 3]

  Phase 3 clinical trial update for Lamazym Aftercare in Alpha-Mannosidosis has completed.

• CLINICAL_TRIALS trial_result · 2023-07-28
  Clinical Trial Update: Lamazym Aftercare Study FR Designed to Provide Treatment for French Patients [Phase 3]

  Phase 3 clinical trial update for Lamazym Aftercare in French patients with Alpha-Mannosidosis has completed.

• CLINICAL_TRIALS trial_result · 2021-10-26
  Clinical Trial Update: Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis [Phase 2]

  Phase 2 trial update on velmanase alfa for pediatric alpha-mannosidosis completed, reporting safety and efficacy findings.

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• CLINICAL_TRIALS trial_result · 2020-11-20
  Clinical Trial Update: Evaluation of Long-term Efficacy of Treatment With Lamazym [Phase 3]

  Phase 3 trial evaluating long-term efficacy of Lamazym in Alpha-Mannosidosis has completed.

• CLINICAL_TRIALS trial_result · 2020-08-03
  Clinical Trial Update: A Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-Mannosidosis [Phase 3]

  A randomized, placebo-controlled Phase 3 trial evaluating repeated Lamazym treatment in subjects with alpha-mannosidosis has been completed.

• CLINICAL_TRIALS trial_result · 2017-03-29
  Clinical Trial Update: Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis [Phase 2]

  This update summarizes the long-term efficacy and safety results from a Phase 2 study of Lamazym in patients with Alpha-Mannosidosis.

• CLINICAL_TRIALS trial_result · 2012-09-26
  Clinical Trial Update: Dose Finding Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosis [Phase 2]

  Phase 2 dose-finding trial of recombinant human alpha-mannosidase for Alpha-mannosidosis; the status of the study is unknown.