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CLINICAL_TRIALS trial_result · 2021-10-26

Clinical Trial Update: Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis [Phase 2]

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Summary

Phase 2 trial update on velmanase alfa for pediatric alpha-mannosidosis completed, reporting safety and efficacy findings.

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Diseases / indications

Drugs mentioned

  • velmanase alfa (velmanase alfa)

Snippet

Sponsor: Chiesi Farmaceutici S.p.A. | Conditions: Alpha-Mannosidosis | Phase 2 | Status: COMPLETED