CLINICAL_TRIALS
trial_result
· 2021-10-26
Clinical Trial Update: Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis [Phase 2]
Summary
Phase 2 trial update on velmanase alfa for pediatric alpha-mannosidosis completed, reporting safety and efficacy findings.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Chiesi Farmaceutici S.p.A. | Conditions: Alpha-Mannosidosis | Phase 2 | Status: COMPLETED