Alexander Disease
📧 Sign up to get email alerts when something new happens for Alexander Disease.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of Zilganersen (ION373) in Patients With Alexander Disease (AxD) [Phase 3]
A Phase 3 study to evaluate the safety and efficacy of Zilganersen (ION373) in patients with Alexander disease is currently active but not r…
-
CLINICAL_TRIALS research · 2026-03-23Clinical Trial Update: Zilganersen Expanded Access Program for Individuals With Alexander Disease
The document discusses an expanded access program for Zilganersen to treat Alexander disease, sponsored by Ionis Pharmaceuticals. The progra…
-
CLINICAL_TRIALS research · 2026-01-15Clinical Trial Update: Evaluation of Outcome Metrics in Alexander Disease
This document announces a clinical trial evaluating outcome metrics in Alexander disease, sponsored by Children's Hospital of Philadelphia, …
-
CLINICAL_TRIALS research · 2025-10-23Clinical Trial Update: The Myelin Disorders Biorepository Project
This clinical trials update describes the Myelin Disorders Biorepository Project (NCT03047369) from Children’s Hospital of Philadelphia, cur…