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CLINICAL_TRIALS research · 2026-03-23

Clinical Trial Update: Zilganersen Expanded Access Program for Individuals With Alexander Disease

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Summary

The document discusses an expanded access program for Zilganersen to treat Alexander disease, sponsored by Ionis Pharmaceuticals. The program status is AVAILABL…

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Diseases / indications

Drugs mentioned

  • Zilganersen

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Alexander Disease | Status: AVAILABLE