Xiap Deficiency
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: Quercetin in Patients With XIAP (X-linked Inhibitor of Apoptosis) Deficiency [Phase 1]
Phase 1 clinical trial evaluating quercetin in patients with XIAP deficiency; currently recruiting.
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CLINICAL_TRIALS research · 2026-03-03Clinical Trial Update: Study to Evaluate the Efficacy, Safety and Tolerability of MAS825 in Patients With Monogenic IL-18 Driven Autoinflammatory Diseases, Including NLRC4-GOF, XIAP Deficiency, or CDC42 Mutations [Phase 2]
Phase 2 trial update on MAS825 for monogenic IL-18–driven autoinflammatory diseases, including NLRC4-GOF, XIAP deficiency, Autoinflammation …
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CLINICAL_TRIALS trial_result · 2025-07-02Clinical Trial Update: Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency [Phase 3]
A Phase 3 trial of tadekinig alfa for NLRC4-associated macrophage activation syndrome (NLRC4-MAS) and XIAP deficiency has completed with res…
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CLINICAL_TRIALS trial_result · 2025-03-17Clinical Trial Update: Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency As Open Label Extension [Phase 3]
A Phase 3 open-label extension of tadekinig alfa for XIAP deficiency and NLRC4-associated macrophage activation syndrome has completed.