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CLINICAL_TRIALS research · 2026-03-03

Clinical Trial Update: Study to Evaluate the Efficacy, Safety and Tolerability of MAS825 in Patients With Monogenic IL-18 Driven Autoinflammatory Diseases, Including NLRC4-GOF, XIAP Deficiency, or CDC42 Mutations [Phase 2]

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Summary

Phase 2 trial update on MAS825 for monogenic IL-18–driven autoinflammatory diseases, including NLRC4-GOF, XIAP deficiency, Autoinflammation With Infantile Enter…

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Diseases / indications

Drugs mentioned

  • MAS825

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations | Phase 2 | Status: ACTIVE_NOT_RECRUITING