X-linked Myotubular Myopathy
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators [Phase 1, Phase 2]
Astellas Gene Therapies reports that ASP2957 is being studied in male participants with X-linked myotubular myopathy who need ventilators, i…
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
Astellas Gene Therapies is recruiting for a study to monitor liver health in boys with X-Linked Myotubular Myopathy (XLMTM).
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CLINICAL_TRIALS research · 2025-04-09Clinical Trial Update: Myotubular and Centronuclear Myopathy Patient Registry
A patient registry study update for myotubular myopathy and centronuclear myopathy, currently recruiting to collect natural history and outc…