X-linked Myotubular Myopathy
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators [Phase 1, Phase 2]
Astellas Gene Therapies reports that ASP2957 is being studied in male participants with X-linked myotubular myopathy who need ventilators, i…
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
Astellas Gene Therapies is recruiting for a study to monitor liver health in boys with X-Linked Myotubular Myopathy (XLMTM).
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CLINICAL_TRIALS research · 2025-04-09Clinical Trial Update: Myotubular and Centronuclear Myopathy Patient Registry
A patient registry study update for myotubular myopathy and centronuclear myopathy, currently recruiting to collect natural history and outc…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Tamoxifen Therapy for Myotubular Myopathy [Phase 1, Phase 2]
Phase 1/Phase 2 trial of tamoxifen for X-linked myotubular myopathy has terminated.
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CLINICAL_TRIALS trial_result · 2024-08-20Clinical Trial Update: A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM) [Phase 2, Phase 3]
Clinical trial update reporting results for AT132 in young children with X-Linked Myotubular Myopathy across Phase 2 and Phase 3, with resul…
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CLINICAL_TRIALS trial_result · 2018-03-07Clinical Trial Update: Myotubular Myopathy Event Study
A completed study update for X-linked myotubular myopathy from Cure CMD. The snippet does not provide trial results.