Wilson Disease
📧 Sign up to get email alerts when something new happens for Wilson Disease.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: Prescreening Study to Identify Potential Wilson Disease Participants for Gene-Editing Clinical Trial
Prime Medicine is running a prescreening study to identify Wilson disease patients for an upcoming gene-editing clinical trial. The study is…
-
CLINICAL_TRIALS research · 2026-03-13Clinical Trial Update: A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease [Phase 1, Phase 2]
A Phase 1/2/3 trial of UX701 gene therapy for Wilson disease is currently active but not recruiting.
-
CLINICAL_TRIALS research · 2026-03-12Clinical Trial Update: Trientine Tetrahydrochloride Administered Once a Day for the First Line Treatment of Wilson's Disease Patients. [Phase 3]
A Phase 3 trial assessing once-daily trientine tetrahydrochloride as first-line treatment for Wilson's disease is not yet recruiting.
-
CLINICAL_TRIALS research · 2026-03-05Clinical Trial Update: Off Treatment Urinary Copper Excretion in Wilson Disease, Pilot Study
A Yale University pilot study is examining urinary copper excretion in Wilson disease patients off treatment and is currently recruiting.
-
CLINICAL_TRIALS research · 2026-01-23Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of LY-M003 Injection in Patients With Wilson Disease [EARLY_Phase 1]
An early-phase 1 clinical trial evaluating the safety and potential efficacy of LY-M003 injections in Wilson disease is currently recruiting…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2026-01-23Clinical Trial Update: Wilson's Disease Treated With D-Penicillamine: Characterization of Skin Damage Secondary to Treatment by Measuring Skin Elasticity [NA]
This clinical trial investigates skin elasticity in Wilson disease patients treated with D-penicillamine to characterize treatment-related s…
-
CLINICAL_TRIALS research · 2026-01-20Clinical Trial Update: A Clinical Study on the Treatment of Wilson Disease With ATP7B mRNA/LNP (DSL101) [EARLY_Phase 1]
EARLY Phase 1 clinical trial update for DSL101, an ATP7B mRNA/LNP therapy for Wilson disease, currently recruiting.
-
CLINICAL_TRIALS research · 2026-01-15Clinical Trial Update: Circadian Variation of Urinary Copper Excretion in Wilson Disease Patients
A clinical trial update from Hospices Civils de Lyon investigating circadian variation of urinary copper excretion in Wilson disease patient…
-
CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Oral Health and Wilson's Disease: SOMAWI
This clinical trial update indicates that the SOMAWI study on oral health in Wilson disease is currently recruiting.
-
CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Cardiac Involvement in Wilson's Disease [NA]
A clinical trial investigating cardiac involvement in Wilson disease is currently recruiting.
-
CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Description of the Copper Concentration in Breast Milk in Women Treated for Wilson's Disease [NA]
A clinical trial update indicates recruitment for a study measuring copper concentration in breast milk of women treated for Wilson's Diseas…
-
CLINICAL_TRIALS research · 2025-12-10Clinical Trial Update: Description of Renal Involvement in Wilson's Disease
A clinical trial update focusing on renal involvement in Wilson disease, with the study not yet recruiting.
-
CLINICAL_TRIALS research · 2025-11-21Clinical Trial Update: Multifaceted Assessment of Patients With Wilson's Disease in a Low-Resource Setting in Upper Egypt: Service Integration, Psychosocial Burden, Dietary Practices, and the Geo-Spatial Disease Map
An upcoming protocol at Assiut University in Upper Egypt is evaluating multifaceted assessments for Wilson's disease, including service inte…
-
CLINICAL_TRIALS research · 2025-10-06Clinical Trial Update: Endocrine Dysfunction in Pediatric Wilson's Disease
A clinical trial sponsored by Assiut University investigating endocrine dysfunction in pediatric Wilson's disease, currently not yet recruit…
-
CLINICAL_TRIALS research · 2025-09-08Clinical Trial Update: Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT
An ongoing clinical trial is evaluating a gene therapy for Wilson disease, using 64Cu PET/CT imaging to assess copper metabolism.
-
CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: International Wilson's Disease Patient Registry (iWilson Registry)
Ongoing recruitment for the International Wilson disease Patient Registry (iWilson Registry) sponsored by Orphalan.
-
CLINICAL_TRIALS research · 2025-05-22Clinical Trial Update: Natural History of Wilson Disease
A Yale-sponsored clinical study is currently recruiting to characterize the natural history of Wilson disease.
-
CLINICAL_TRIALS research · 2025-05-01Clinical Trial Update: ExAblate Transcranial MRgFUS for the Management of Treatment-Refractory Movement Disorders [NA]
Clinical trial update on ExAblate Transcranial MRgFUS for treatment-refractory movement disorders; the study is currently active but not rec…
-
CLINICAL_TRIALS research · 2024-12-05Clinical Trial Update: French Wilson Disease Registry
This clinical trials registry entry indicates the Wilson disease study NCT05231876 is currently recruiting, sponsored by Fondation Ophtalmol…
-
CLINICAL_TRIALS research · 2024-11-21Clinical Trial Update: Daily Versus Alternate Day Plasma Exchange in Wilson Disease With Acute Liver Failure in Children [NA]
A clinical trial is evaluating daily versus alternate-day plasma exchange in children with Wilson disease and acute liver failure; the study…
-
CLINICAL_TRIALS research · 2024-10-29Clinical Trial Update: An Exploratory Study to Evaluate the Tolerability and Safety of MWAV201 in Subjects With Wilson Disease [NA]
An exploratory clinical trial evaluating the tolerability and safety of MWAV201 in individuals with Wilson disease; the study is sponsored b…
-
CLINICAL_TRIALS research · 2024-06-20Clinical Trial Update: Spanish Wilson Disease Registry
A Spanish Wilson disease registry is currently recruiting participants, sponsored by Asociación Española para el Estudio del Hígado.