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CLINICAL_TRIALS research · 2025-09-08

Clinical Trial Update: Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT

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Summary

An ongoing clinical trial is evaluating a gene therapy for Wilson disease, using 64Cu PET/CT imaging to assess copper metabolism.

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Diseases / indications

Drugs mentioned

  • Gene Therapy for Wilson Disease (investigational)

Snippet

Sponsor: Thomas Damgaard Sandahl | Conditions: Wilson Disease | Status: ENROLLING_BY_INVITATION