Records containing: TUBB4A-Related Leukodystrophy
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CLINICAL_TRIALS study record update · 2025-10-29An Open-label, Single Center, Single Participant Study of an Experimental Antisense Oligonucleotide Treatment for TUBB4A-related Leukodystrophy
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CLINICAL_TRIALS study record update · 2025-10-23The Myelin Disorders Biorepository Project and Global Leukodystrophy Initiative Clinical Trials Network
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CLINICAL_TRIALS study record update · 2025-06-15LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies