Scheie Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2016-01-26Clinical Trial Update: A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I [NA]
Clinical trial assessing intrathecal enzyme therapy for cognitive decline in mucopolysaccharidosis type I has completed.
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CLINICAL_TRIALS trial_result · 2014-05-05Clinical Trial Update: A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG (Glycosaminoglycan) Levels in Aldurazyme® Treated Patients [Phase 4]
Phase 4 study investigating the relationship between anti-laronidase antibodies and urinary glycosaminoglycans in Aldurazyme-treated patient…
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CLINICAL_TRIALS trial_result · 2013-02-21Clinical Trial Update: Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I [Phase 1]
Extension study of intrathecal enzyme replacement therapy for Mucopolysaccharidosis Type I (Phase 1) has been terminated. The trial involved…
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CLINICAL_TRIALS trial_result · 2009-06-16Clinical Trial Update: A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old [Phase 2]
Phase 2 study evaluating the safety and pharmacokinetics of Aldurazyme (laronidase) in patients under 5 years old with mucopolysaccharidosis…
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CLINICAL_TRIALS trial_result · 2009-06-16Clinical Trial Update: Phase 3 Extension Study of the Safety and Efficacy of Aldurazyme® (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients [Phase 3]
This Phase 3 extension study evaluated the safety and efficacy of Aldurazyme (laronidase) in patients with Mucopolysaccharidosis I and has c…
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CLINICAL_TRIALS trial_result · 2009-06-16Clinical Trial Update: A Dose-optimization Study of Aldurazyme® (Laronidase) in Patients With Mucopolysaccharidosis I (MPS I) Disease [Phase 4]
Phase 4 dose-optimization study of Aldurazyme (Laronidase) in patients with Mucopolysaccharidosis I completed with results posted in 2009.
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CLINICAL_TRIALS trial_result · 2009-02-12Clinical Trial Update: Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease [Phase 3]
Phase 3 study of Aldurazyme (laronidase) for mucopolysaccharidosis I has completed, with results posted in 2009.