Clinical Trial Update: Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I [Phase 1]

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Summary

Extension study of intrathecal enzyme replacement therapy for Mucopolysaccharidosis Type I (Phase 1) has been terminated. The trial involved patients with spina…

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Diseases / indications

• Hurler Syndrome
• Hurler-scheie Syndrome
• Mucopolysaccharidosis Type
• Scheie Syndrome

Drugs mentioned

• Aldurazyme (Laronidase)

Snippet

Sponsor: Patricia I. Dickson, M.D. | Conditions: Spinal Cord Compression, Mucopolysaccharidosis I | Phase 1 | Status: TERMINATED