Progressive Familial Intrahepatic Cholestasis

• CLINICAL_TRIALS trial_result · 2026-06-23
  Clinical Trial Results: An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC) [Phase 3]

  Phase 3 extension study results for maralixibat in Progressive Familial Intrahepatic Cholestasis (PFIC) have been completed with results pos…

• CLINICAL_TRIALS trial_result · 2026-06-02
  Clinical Trial Results: A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS). [Phase 2]

  Phase 2 study evaluating safety and tolerability of maralixibat in infants with cholestatic liver diseases including PFIC and Alagille syndr…

• CLINICAL_TRIALS trial_result · 2026-02-20
  Clinical Trial Update: A Database Study of Maralixibat (TAK-625) in Participants With Alagille Syndrome (ALGS) and Progressive Familial Intrahepatic Cholestasis (PFIC)

  This clinical trial status update describes a database study evaluating maralixibat (TAK-625) in participants with Alagille syndrome and pro…

• CLINICAL_TRIALS trial_result · 2025-07-10
  Clinical Trial Update: Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC [Phase 3]

  A4250 (odevixibat) was studied in a long-term Phase 3 trial in children with Progressive Familial Intrahepatic Cholestasis. The results asse…

• CLINICAL_TRIALS trial_result · 2025-06-29
  Clinical Trial Update: An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC) [Phase 3]

  Clinical trial update announcing completion of an extension study of maralixibat in patients with Progressive Familial Intrahepatic Cholesta…

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• CLINICAL_TRIALS trial_result · 2025-02-06
  Clinical Trial Update: A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS). [Phase 2]

  Phase 2 trial evaluating the safety and tolerability of maralixibat in infant participants with progressive familial intrahepatic cholestasi…

• CLINICAL_TRIALS trial_result · 2024-09-24
  Clinical Trial Update: A Study of TAK-625 for the Treatment of Progressive Familial Intrahepatic Cholestasis (PFIC) [Phase 3]

  A Phase 3 study evaluating TAK-625 for Progressive Familial Intrahepatic Cholestasis has completed and posted results.

• CLINICAL_TRIALS trial_result · 2023-12-11
  Clinical Trial Update: A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC) [Phase 3]

  Phase 3 trial evaluating maralixibat for progressive familial intrahepatic cholestasis has completed with results posted.

• CLINICAL_TRIALS trial_result · 2021-07-12
  Clinical Trial Update: Open Label Study to Evaluate Efficacy and Long Term Safety of LUM001 (Maralixibat) in the Treatment of Cholestatic Liver Disease in Patients With Progressive Familial Intrahepatic Cholestasis [Phase 2]

  Phase 2 open-label study evaluating efficacy and long-term safety of LUM001 (maralixibat) in progressive familial intrahepatic cholestasis h…