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CLINICAL_TRIALS trial_result · 2025-06-29

Clinical Trial Update: An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC) [Phase 3]

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Summary

Clinical trial update announcing completion of an extension study of maralixibat in patients with Progressive Familial Intrahepatic Cholestasis (PFIC) in Phase …

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Diseases / indications

Drugs mentioned

  • Maralixibat (maralixibat)

Snippet

Sponsor: Mirum Pharmaceuticals, Inc. | Conditions: Progressive Familial Intrahepatic Cholestasis (PFIC) | Phase 3 | Status: COMPLETED