Platelet Storage Pool Deficiency
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2013-08-02Clinical Trial Update: Pilot Study of a Multi-Drug Regimen for Severe Pulmonary Fibrosis in Hermansky-Pudlak Syndrome [Phase 1, Phase 2]
This clinical trial evaluated a multi-drug regimen for severe pulmonary fibrosis in Hermansky-Pudlak Syndrome (a rare genetic disorder); the…
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CLINICAL_TRIALS trial_result · 2012-01-26Clinical Trial Update: Oral Pirfenidone for the Pulmonary Fibrosis of Hermansky-Pudlak Syndrome [Phase 2]
Phase 2 trial of oral pirfenidone for Hermansky-Pudlak syndrome-associated pulmonary fibrosis has completed and results have been posted. Th…