Clinical Trial Update: Pilot Study of a Multi-Drug Regimen for Severe Pulmonary Fibrosis in Hermansky-Pudlak Syndrome [Phase 1, Phase 2]

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Summary

This clinical trial evaluated a multi-drug regimen for severe pulmonary fibrosis in Hermansky-Pudlak Syndrome (a rare genetic disorder); the Phase 1/2 study was…

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Diseases / indications

• Hermansky-pudlak Syndrome
• Metabolic Disease
• Oculocutaneous Albinism
• Platelet Storage Pool Deficiency
• Pulmonary Fibrosis

Snippet

Sponsor: National Human Genome Research Institute (NHGRI) | Conditions: Hermansky-Pudlak Syndrome (HPS), Pulmonary Fibrosis | Phase 1, Phase 2 | Status: TERMINATED | Results posted: 2013-08-02