Pantothenate Kinase-associated Neurodegeneration
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Deep Brain Stimulation (DBS) MatchMaker
Boston Children's Hospital reports an ongoing Deep Brain Stimulation MatchMaker trial enrolling by invitation for multiple genetic movement …
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CLINICAL_TRIALS trial_result · 2025-10-29Clinical Trial Update: CoA-Z in Pantothenate Kinase-associated Neurodegeneration (PKAN) [NA]
Clinical trial evaluating CoA-Z in Pantothenate Kinase-associated Neurodegeneration has completed and posted results.
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CLINICAL_TRIALS research · 2025-06-05Clinical Trial Update: TIRCON International NBIA Registry
The TIRCON International NBIA Registry is actively recruiting participants to collect clinical and translational data on neurodegeneration w…
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CLINICAL_TRIALS trial_result · 2020-12-29Clinical Trial Update: Efficacy and Safety Study of Fosmetpantotenate (RE-024) in PKAN Participants [Phase 3]
Phase 3 efficacy and safety study of fosmetpantotenate (RE-024) in Pantothenate Kinase-Associated Neurodegeneration (PKAN) was terminated.
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EMA withdrawal · 2020-10-28EMA Application withdrawn: Upkanz (Deferiprone) — Apotex B.V.
The EMA has withdrawn the application for Upkanz (deferiprone) by Apotex B.V. for Pantothenate Kinase-Associated Neurodegeneration.
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CLINICAL_TRIALS trial_result · 2019-07-17Clinical Trial Update: Long-term Deferiprone Treatment in Patients With Pantothenate Kinase-Associated Neurodegeneration [Phase 3]
Phase 3 trial evaluating long-term deferiprone treatment in Pantothenate Kinase-Associated Neurodegeneration has completed with results post…
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CLINICAL_TRIALS trial_result · 2019-05-23Clinical Trial Update: Efficacy and Safety Study of Deferiprone in Patients With Pantothenate Kinase-associated Neurodegeneration (PKAN) [Phase 3]
Phase 3 trial update on deferiprone for Pantothenate Kinase-associated Neurodegeneration (PKAN) with completed status and results posted.
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CLINICAL_TRIALS trial_result · 2018-05-29Clinical Trial Update: Brain Perfusion in Pantothenate Kinase-associated Neurodegeneration (PKAN)
Clinical trial evaluating brain perfusion for Pantothenate Kinase-associated Neurodegeneration (PKAN) has completed.