Oculopharyngeal Muscular Dystrophy
📧 Sign up to get email alerts when something new happens for Oculopharyngeal Muscular Dystrophy.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2019-07-17Clinical Trial Update: Continuation Protocol to Protocol BBCO-001 [Phase 3]
Phase 3 continuation protocol update for BBCO-001 in oculopharyngeal muscular dystrophy (OPMD) has completed.
-
CLINICAL_TRIALS trial_result · 2017-08-23Clinical Trial Update: Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients [Phase 2]
A Phase 2 study evaluating Cabaletta for safety, tolerability, and efficacy in oculopharyngeal muscular dystrophy has completed, with result…
-
CLINICAL_TRIALS trial_result · 2015-11-20Clinical Trial Update: Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts [Phase 2]
A completed Phase 2 trial investigating autologous myoblast transplantation to treat dysphagia in patients with oculopharyngeal muscular dys…
-
CLINICAL_TRIALS trial_result · 2008-03-04Clinical Trial Update: Study of Muscle Abnormalities in Patients With Specific Genetic Mutations
An NHLBI-sponsored clinical trial evaluating muscle abnormalities in patients with specific genetic mutations has completed.