Oculopharyngeal Muscular Dystrophy
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CLINICAL_TRIALS research · 2026-01-27Clinical Trial Update: Oral Health, Saliva Viscosity and Composition in Oculo-Pharyngeal Muscular Dystrophy (OPMD)
This clinical trial aims to study oral health, saliva viscosity, and saliva composition in individuals with oculopharyngeal muscular dystrop…
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CLINICAL_TRIALS research · 2025-12-31Clinical Trial Update: A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating the safety and potential activity of intramuscular BB-301 in individuals with oculopharyngeal muscu…
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CLINICAL_TRIALS research · 2025-08-28Clinical Trial Update: Natural History of Oculo-Pharyngeal Muscular Dystrophy (OPMD) - Israel National OPMD Registry
This clinical trial update describes the Israel National OPMD Registry study focused on the natural history of oculopharyngeal muscular dyst…
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CLINICAL_TRIALS trial_result · 2019-07-17Clinical Trial Update: Continuation Protocol to Protocol BBCO-001 [Phase 3]
Phase 3 continuation protocol update for BBCO-001 in oculopharyngeal muscular dystrophy (OPMD) has completed.
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CLINICAL_TRIALS trial_result · 2017-08-23Clinical Trial Update: Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients [Phase 2]
A Phase 2 study evaluating Cabaletta for safety, tolerability, and efficacy in oculopharyngeal muscular dystrophy has completed, with result…
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CLINICAL_TRIALS trial_result · 2015-11-20Clinical Trial Update: Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts [Phase 2]
A completed Phase 2 trial investigating autologous myoblast transplantation to treat dysphagia in patients with oculopharyngeal muscular dys…
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CLINICAL_TRIALS research · 2014-06-06Clinical Trial Update: Effect of Aerobic Training in Patients With Oculopharyngeal Muscular Dystrophy [NA]
A study is evaluating the effects of aerobic training in patients with oculopharyngeal muscular dystrophy; no results or current status are …
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CLINICAL_TRIALS research · 2010-07-22Clinical Trial Update: Dysphagia in Oculopharyngeal Muscular Dystrophy (OPMD)- Evaluation, Endoscopic Examination of Swallowing, Treatment and Long Term Follow up [Phase 1]
This is a Phase 1 clinical trial evaluating swallowing assessment and treatment options for dysphagia in patients with oculopharyngeal muscu…
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CLINICAL_TRIALS trial_result · 2008-03-04Clinical Trial Update: Study of Muscle Abnormalities in Patients With Specific Genetic Mutations
An NHLBI-sponsored clinical trial evaluating muscle abnormalities in patients with specific genetic mutations has completed.