Niemann-pick Disease Type C1
📧 Sign up to get email alerts when something new happens for Niemann-pick Disease Type C1.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Functional Near-Infrared Spectroscopy (fNIRS) Combined With Diffuse Correlation Spectroscopy (DCS) in Neurocognitive Disease as Compared to Healthy Neurotypical Controls
Status update on a completed clinical trial evaluating functional near-infrared spectroscopy combined with diffuse correlation spectroscopy …
-
CLINICAL_TRIALS trial_result · 2022-08-30Clinical Trial Update: Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1 [Phase 1, Phase 2]
Phase 1/2 trial investigating combined intrathecal and intravenous VTS-270 for Niemann-Pick disease type C1 was terminated with results post…
-
CLINICAL_TRIALS trial_result · 2018-02-22Clinical Trial Update: Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1 [Phase 1, Phase 2]
Phase 1/2 trial of vorinostat for Niemann-Pick Disease Type C1 completed with results posted in 2018.