Niemann-pick Disease Type C1
📧 Sign up to get email alerts when something new happens for Niemann-pick Disease Type C1.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2024-06-04Clinical Trial Update: Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1 [Phase 3]
A Phase 3 trial update for intravenous Trappsol Cyclo in pediatric and adult Niemann-Pick disease type C1 patients; the study is currently a…