Neurodevelopmental Disorder with or Without Variable Brain Abnormalities
📧 Sign up to get email alerts when something new happens for Neurodevelopmental Disorder with or Without Variable Brain Abnormalities.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2025-09-29Clinical Trial Update: Personalized Antisense Oligonucleotide for a Single Participant With MAPK8IP3 Neurodevelopmental Disorder With or Without Variable Brain Abnormalities (NEDBA) [Phase 1, Phase 2]
An update on a Phase 1/Phase 2, personalized antisense oligonucleotide trial for a single participant with MAPK8IP3-related neurodevelopment…