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CLINICAL_TRIALS trial_result · 2025-09-29

Clinical Trial Update: Personalized Antisense Oligonucleotide for a Single Participant With MAPK8IP3 Neurodevelopmental Disorder With or Without Variable Brain Abnormalities (NEDBA) [Phase 1, Phase 2]

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Summary

An update on a Phase 1/Phase 2, personalized antisense oligonucleotide trial for a single participant with MAPK8IP3-related neurodevelopmental disorder with or …

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Diseases / indications

Drugs mentioned

  • Personalized antisense oligonucleotide targeting MAPK8IP3 (antisense oligonucleotide)

Snippet

Sponsor: n-Lorem Foundation | Conditions: Neurodevelopmental Disorder With or Without Variable Brain Abnormalities | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING