Mucopolysaccharidosis Type Iiib
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CLINICAL_TRIALS research · 2025-09-02Clinical Trial Update: An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB [Phase 1, Phase 2]
An open-label Phase 1/2 study of JR-446 for the treatment of Mucopolysaccharidosis type IIIB is currently recruiting.
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CLINICAL_TRIALS research · 2017-02-03Clinical Trial Update: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB
A completed retrospective chart review describing deceased patients with Mucopolysaccharidosis Type IIIB (Sanfilippo syndrome).