Clinical Trial Update: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB

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Summary

A completed retrospective chart review describing deceased patients with Mucopolysaccharidosis Type IIIB (Sanfilippo syndrome).

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Diseases / indications

• Mucopolysaccharidosis Type Iiib

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: MPS IIIB (Sanfilippo Syndrome) | Status: COMPLETED