Mucopolysaccharidosis Type 7
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CLINICAL_TRIALS research · 2017-02-06Clinical Trial Update: An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patient
An open-label treatment protocol update for an advanced-stage patient with Mucopolysaccharidosis Type 7 treated with UX003 rhGUS enzyme repl…