Clinical Trial Update: An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patient

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Summary

An open-label treatment protocol update for an advanced-stage patient with Mucopolysaccharidosis Type 7 treated with UX003 rhGUS enzyme replacement therapy.

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Diseases / indications

• Mucopolysaccharidosis Type 7

Drugs mentioned

• UX003 rhGUS enzyme replacement therapy (recombinant human beta-glucuronidase)

Snippet

Sponsor: Joyce Fox | Conditions: Mucopolysaccharidosis Type 7 | Status: NO_LONGER_AVAILABLE