Mitochondrial Metabolism Defect
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CLINICAL_TRIALS trial_result · 2025-10-24Clinical Trial Update: Study to Evaluate Efficacy and Safety of Elamipretide in Subjects With Primary Mitochondrial Disease From Nuclear DNA Mutations (nPMD) [Phase 3]
Phase 3 study evaluating the efficacy and safety of elamipretide in subjects with primary mitochondrial disease from nuclear DNA mutations h…