Lysosomal Storage Disorders
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Genetic Studies of Lysosomal Storage Disorders
A genetic study of lysosomal storage disorders, including Gaucher disease and potentially Parkinson disease, is currently enrolling by invit…
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CLINICAL_TRIALS research · 2017-04-04Clinical Trial Update: Investigating Lysosomal Storage Diseases in Minority Groups
A clinical trial update from O & O Alpan LLC examining lysosomal storage disorders in minority populations, including Gaucher disease, Fabry…